Antisense oligonucleotide (ASO) drugs represent a significant branch of the small nucleic acid therapeutic field, functioning as molecules that regulate gene expression through specific binding to mRNA.
Levicept Unveils Promising Phase II Results for LEVI-04, a New Neurotrophin-3 Inhibitor, in Treating Moderate to Severe Osteoarthritis at ACR Convergence 2024.
This opinion endorses the approval of the amyloid-beta (Aβ) monoclonal antibody lecanemab for adult patients diagnosed with mild cognitive impairment and mild dementia due to Alzheimer's disease.
Spirovant Sciences has administered the first dose to a patient in the SAAVe Phase 1/2 trial for its experimental aerosol-based genetic treatment for cystic fibrosis.
Pirtobrutinib is a small molecule drug developed by Redx Pharma Plc, targeting BTK C481S. Pirtobrutinib has received its first approval in the United States.